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B. Monia · SciRah

Researcher profile · Semantic Scholar

B. Monia

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B. Monia — researcher profile on SciRah

h-index: 82
Works: 325
Citations: 26K

Most-cited papers

Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis
M. Benson, M. Waddington‐Cruz, J. Berk, M. Polydefkis +31 more
2018New England Journal of Medicine769 citations Open access
Semantic Scholar
Nicotinamide N-methyltransferase knockdown protects against diet-induced obesity
D. Kraus, Qin Yang, D. Kong, Alexander S. Banks +15 more
2014Nature446 citations Open access
Semantic Scholar
Peripheral androgen receptor gene suppression rescues disease in mouse models of spinal and bulbar muscular atrophy
A. Lieberman, Zhi-Gang Yu, Sue Murray, Raechel Q Peralta +8 more
2014Cell Reports166 citations Open access
Semantic Scholar
Targeted delivery of antisense oligonucleotides to pancreatic β-cells
Carina Ämmälä, W. Drury, L. Knerr, I. Ahlstedt +16 more
2018Science Advances160 citations Open access
Semantic Scholar
Targeting KRAS-dependent tumors with AZD4785, a high-affinity therapeutic antisense oligonucleotide inhibitor of KRAS
Sarah J. Ross, Alexey S. Revenko, Lyndsey Hanson, Rebecca P A Ellston +13 more
2017Science Translational Medicine158 citations Open access
Semantic Scholar
Suppressing transthyretin production in mice, monkeys and humans using 2nd-Generation antisense oligonucleotides
E. J. Ackermann, Shuling Guo, M. Benson, Sheri L. Booten +9 more
2016Amyloid: Journal of Protein Folding Disorders130 citations
Semantic Scholar
Generation 2.5 Antisense Oligonucleotides Targeting the Androgen Receptor and Its Splice Variants Suppress Enzalutamide-Resistant Prostate Cancer Cell Growth
Y. Yamamoto, Y. Loriot, E. Beraldi, Fan Zhang +12 more
2015Clinical Cancer Research120 citations Open access
Semantic Scholar
Platelet-localized FXI promotes a vascular coagulation-inflammatory circuit in arterial hypertension
Sabine Kossmann, J. Lagrange, Sven Jäckel, K. Jurk +20 more
2017Science Translational Medicine119 citations
Semantic Scholar
Colon Cancer Growth and Dissemination Relies upon Thrombin, Stromal PAR-1, and Fibrinogen
Gregory N. Adams, L. Rosenfeldt, Malinda D. Frederick, W. Miller +7 more
2015Cancer Research110 citations Open access
Semantic Scholar
An oral antisense oligonucleotide for PCSK9 inhibition
Peter Gennemark, Katrin Walter, N. Clemmensen, D. Rekić +24 more
2021Science Translational Medicine109 citations
Semantic Scholar
Allele-Specific Inhibition of Rhodopsin With an Antisense Oligonucleotide Slows Photoreceptor Cell Degeneration.
S. Murray, A. Jazayeri, M. Matthes, D. Yasumura +10 more
2015Investigative Ophthalmology and Visual Science97 citations Open access
Semantic Scholar
Antisense oligonucleotide treatment ameliorates IFN-γ-induced proteinuria in APOL1-transgenic mice.
M. Aghajan, Sheri L. Booten, M. Althage, Christopher E. Hart +13 more
2019JCI Insight95 citations Open access
Semantic Scholar
Antisense oligonucleotide-mediated Dnm2 knockdown prevents and reverts myotubular myopathy in mice
H. Tasfaout, S. Buono, Shuling Guo, C. Kretz +6 more
2017Nature Communications90 citations Open access
Semantic Scholar
Ligand conjugated antisense oligonucleotide for the treatment of transthyretin amyloidosis: preclinical and phase 1 data
N. Viney, Shuling Guo, Li-Jung Tai, B. Baker +14 more
2020ESC Heart Failure83 citations Open access
Semantic Scholar
Thrombin Signaling Promotes Pancreatic Adenocarcinoma through PAR-1–Dependent Immune Evasion
Yi Yang, Amanda Stang, P. Schweickert, N. Lanman +9 more
2019Cancer Research79 citations Open access
Semantic Scholar
Inhaled ENaC antisense oligonucleotide ameliorates cystic fibrosis-like lung disease in mice.
J. Crosby, Chenguang Zhao, Chong Jiang, D. Bai +7 more
2017Journal of Cystic Fibrosis79 citations Open access
Semantic Scholar
Combination of Tmprss6- ASO and the iron chelator deferiprone improves erythropoiesis and reduces iron overload in a mouse model of beta-thalassemia intermedia
C. Casu, M. Aghajan, Paraskevi Rea Oikonomidou, Shuling Guo +2 more
2016Haematologica78 citations Open access
Semantic Scholar
Antisense oligonucleotide treatment ameliorates alpha-1 antitrypsin-related liver disease in mice.
Shuling Guo, Sheri L. Booten, M. Aghajan, G. Hung +8 more
2014Journal of Clinical Investigation74 citations Open access
Semantic Scholar
Reducing dynamin 2 (DNM2) rescues DNM2-related dominant centronuclear myopathy
S. Buono, J. Ross, H. Tasfaout, Y. Levy +10 more
2018Proceedings of the National Academy of Sciences of the United States of America59 citations Open access
Semantic Scholar
Nonsense Mediated RNA Decay Pathway Inhibition Restores Expression and Function of W1282X CFTR.
M. M. Keenan, Lulu Huang, N. Jordan, E. Wong +8 more
2019American Journal of Respiratory Cell and Molecular Biology57 citations
Semantic Scholar
Genetic diminution of circulating prothrombin ameliorates multiorgan pathologies in sickle cell disease mice.
P. Arumugam, E. Mullins, S. Shanmukhappa, B. Monia +6 more
2015Blood57 citations Open access
Semantic Scholar
Factor XI Regulates Pathological Thrombus Formation on Acutely Ruptured Atherosclerotic Plaques
M. V. van Montfoort, M. Kuijpers, V. L. Knaup, S. Bhanot +4 more
2014Arteriosclerosis, Thrombosis and Vascular Biology53 citations Open access
Semantic Scholar
Arterial thrombosis is accelerated in mice deficient in histidine-rich glycoprotein.
Trang T. T. Vu, Ji Zhou, B. Leslie, A. Stafford +8 more
2015Blood52 citations Open access
Semantic Scholar
Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-LRx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
T. Coelho, Y. Ando, M. Benson, J. Berk +18 more
2021Neurological Therapeutics51 citations Open access
Semantic Scholar
Antisense suppression of the nonsense mediated decay factor Upf3b as a potential treatment for diseases caused by nonsense mutations
Lulu Huang, Audrey Low, S. Damle, M. M. Keenan +4 more
2018Genome Biology50 citations Open access
Semantic Scholar
Steric Inhibition of 5′ UTR Regulatory Elements Results in Upregulation of Human CFTR
S. Sasaki, Rachel Sun, Huynh-Hoa Bui, J. Crosby +2 more
2019Molecular Therapy46 citations Open access
Semantic Scholar
Thrombin drives tumorigenesis in colitis-associated colon cancer
B. Turpin, W. Miller, L. Rosenfeldt, K. Kombrinck +9 more
2014Cancer Research39 citations Open access
Semantic Scholar
TMPRSS6 as a Therapeutic Target for Disorders of Erythropoiesis and Iron Homeostasis
T. Ganz, E. Nemeth, S. Rivella, Paul W Goldberg +5 more
2023Advances in Therapy38 citations Open access
Semantic Scholar
Pharmacological targeting of coagulation factor XI mitigates the development of experimental atherosclerosis in low-density lipoprotein receptor-deficient mice
A. Ngo, Kelley R. Jordan, P. Mueller, Matthew W. Hagen +13 more
2021Journal of Thrombosis and Haemostasis35 citations Open access
Semantic Scholar
Antisense Oligonucleotides Targeting Jagged 1 Reduce House Dust Mite-Induced Goblet Cell Metaplasia in the Adult Murine Lung.
Michele Carrer, J. Crosby, Guizhen Sun, Chenguang Zhao +5 more
2020American Journal of Respiratory Cell and Molecular Biology31 citations
Semantic Scholar
Inhibition of the alternative complement pathway by antisense oligonucleotides targeting complement factor B improves lupus nephritis in mice.
Tamar R. Grossman, L. Hettrick, Robert B. Johnson, G. Hung +6 more
2016Immunobiology31 citations Open access
Semantic Scholar
IONIS-PKKRx a Novel Antisense Inhibitor of Prekallikrein and Bradykinin Production
Jason D. Ferrone, G. Bhattacharjee, A. Revenko, Thomas A. Zanardi +10 more
2019Nucleic Acid Therapeutics28 citations Open access
Semantic Scholar
Hepatic thrombopoietin gene silencing reduces platelet count and breast cancer progression in transgenic MMTV-PyMT mice.
Toshiaki Shirai, A. Revenko, J. Tibbitts, A. Ngo +9 more
2019Blood Advances28 citations Open access
Semantic Scholar
Population Pharmacokinetic–Pharmacodynamic Modeling of Inotersen, an Antisense Oligonucleotide for Treatment of Patients with Hereditary Transthyretin Amyloidosis
R. Yu, J. Collins, S. Hall, E. J. Ackermann +4 more
2020Nucleic Acid Therapeutics26 citations Open access
Semantic Scholar
Inotersen (transthyretin-specific antisense oligonucleotide) for treatment of transthyretin amyloidosis.
M. Benson, N. Dasgupta, B. Monia
2019Neurodegenerative Disease Management26 citations
Semantic Scholar
Immunogenicity Assessment of Inotersen, a 2′-O-(2-Methoxyethyl) Antisense Oligonucleotide in Animals and Humans: Effect on Pharmacokinetics, Pharmacodynamics, and Safety
R. Yu, Yanfeng Wang, D. Norris, Tae-Won Kim +4 more
2020Nucleic Acid Therapeutics25 citations
Semantic Scholar
Targeting Translation Termination Machinery with Antisense Oligonucleotides for Diseases Caused by Nonsense Mutations
Lulu Huang, M. Aghajan, Tianna Quesenberry, Audrey Low +3 more
2019Nucleic Acid Therapeutics25 citations Open access
Semantic Scholar
Hereditary transthyretin amyloidosis: baseline characteristics of patients in the NEURO-TTR trial
M. Waddington‐Cruz, E. J. Ackermann, M. Polydefkis, S. Heitner +13 more
2018Amyloid: Journal of Protein Folding Disorders24 citations Open access
Semantic Scholar
Partial Hepatectomy Induced Long Noncoding RNA Inhibits Hepatocyte Proliferation during Liver Regeneration
Lulu Huang, S. Damle, Sheri L. Booten, Priyam Singh +9 more
2015PLoS ONE24 citations Open access
Semantic Scholar
CFTR mRNAs with nonsense codons are degraded by the SMG6-mediated endonucleolytic pathway
E. Sanderlin, M. M. Keenan, M. Mense, A. Revenko +3 more
202123 citations Open access
Semantic Scholar
Role for Cela1 in Postnatal Lung Remodeling and Alpha‐1 Antitrypsin‐Deficient Emphysema
R. Joshi, A. Heinz, Q. Fan, Shuling Guo +6 more
2018American Journal of Respiratory Cell and Molecular Biology22 citations Open access
Semantic Scholar
Reduction in ocular complement factor B protein in mice and monkeys by systemic administration of factor B antisense oligonucleotide
Tamar R. Grossman, Michele Carrer, Lijiang Shen, Robert B. Johnson +4 more
2016Molecular Vision21 citations
Semantic Scholar
Evaluation of Therapeutic Oligonucleotides for Familial Amyloid Polyneuropathy in Patient-Derived Hepatocyte-Like Cells
C. Niemietz, V. Sauer, J. Stella, L. Fleischhauer +9 more
2016PLoS ONE21 citations Open access
Semantic Scholar
Antisense oligonucleotide targeting of mRNAs encoding ENaC subunits α, β, and γ improves cystic fibrosis-like disease in mice.
Chenguang Zhao, J. Crosby, Ting-Hong Lv, D. Bai +2 more
2019Journal of Cystic Fibrosis20 citations Open access
Semantic Scholar
Targeting the contact system in a rabbit model of extracorporeal membrane oxygenation
J. Tweddell, Mousa Kharnaf, F. Zafar, K. Riggs +9 more
2022Blood Advances16 citations Open access
Semantic Scholar
In Vitro and In Vivo Effects of SerpinA1 on the Modulation of Transthyretin Proteolysis
Filipa Bezerra, C. Niemietz, H. Schmidt, A. Zibert +5 more
2021International Journal of Molecular Sciences14 citations Open access
Semantic Scholar
Transmembrane Protease, Serine 6 (TMPRSS6) Antisense Oligonucleotide (IONIS-TMPRSS6-LRX) Reduces Plasma Iron Levels of Healthy Volunteers in a Phase 1 Clinical Study
M. Mccaleb, J. Lickliter, A. Dibble, E. Schneider +5 more
2018Blood13 citations Open access
Semantic Scholar
Treatment of transthyretin cardiomyopathy with a TTR-specific antisense oligonucleotide (IONIS-TTRRx)
M. Benson, E. J. Ackermann, B. Monia
2017Amyloid: Journal of Protein Folding Disorders12 citations
Semantic Scholar
Use of antisense oligonucleotides to correct the splicing error in ISCU myopathy patient cell lines.
Gregory P. Holmes-Hampton, D. Crooks, R. Haller, Shuling Guo +3 more
2016Human Molecular Genetics12 citations Open access
Semantic Scholar
Abstract 2713: Discovery and characterization of AZD8701, a high affinity antisense oligonucleotide targeting FOXP3 to relieve immunosuppression in cancer
C. Sinclair, A. Revenko, Robert B. Johnson, A. Peter +15 more
2019Clinical research11 citations
Semantic Scholar

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M. Benson×7
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E. J. Ackermann×6

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