Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial
S. Russell, J. Bennett, J. Wellman, D. Chung +32 more
Researcher profile · Semantic Scholar
S. Russell, J. Bennett, J. Wellman, D. Chung +32 more
E. Sohn, H. W. van Dijk, C. Jiao, P. Kok +13 more
A. Cideciyan, S. Jacobson, A. Drack, A. Ho +23 more
K. Chirco, E. Sohn, Edwin M. Stone, B. Tucker +1 more
P. Campochiaro, A. Lauer, E. Sohn, T. A. Mir +6 more
Erin R. Burnight, Manav Gupta, L. A. Wiley, K. Anfinson +14 more
S. Russell, A. Drack, A. Cideciyan, S. Jacobson +28 more
M. Abràmoff, P. Fort, Ian C. Han, K. T. Jayasundera +2 more
Andrew E. Pouw, Mark A. Greiner, R. Coussa, C. Jiao +5 more
Brian J. Green, K. Worthington, Jessica R. Thompson, Spencer J. Bunn +9 more
E. Sohn, Miles J. Flamme-Wiese, S. Whitmore, G. Workalemahu +8 more
Jessica R. Thompson, K. Worthington, Brian J. Green, Nathaniel K. Mullin +10 more
She-Min Zeng, S. Whitmore, E. Sohn, M. Riker +5 more
L. A. Wiley, Erin R. Burnight, Emily E. Kaalberg, C. Jiao +9 more
Sun-Young Lee, Justine L. Cheng, K. Gehrs, J. Folk +5 more
Ian C. Han, Justine L. Cheng, Erin R. Burnight, Christy L Ralston +9 more
E. Chin, David R. P. Almeida, C. N. Roybal, Philip I. Niles +5 more
E. Sohn, Kai Wang, S. Thompson, M. Riker +3 more
Brittni A Scruggs, C. Jiao, C. Cranston, Emily E. Kaalberg +7 more
E. Sohn, Miles J. Flamme-Wiese, S. Whitmore, Kai Wang +2 more
T. Tien, T. Muto, Joyce Zhang, E. Sohn +2 more
B. Fenner, Jonathan F. Russell, A. Drack, A. Dumitrescu +8 more
Ian C. Han, Erin R. Burnight, Mallory J Ulferts, K. Worthington +6 more
B. Antony, Woojin Jeong, M. Abràmoff, Joseph Vance +2 more
Justine L. Cheng, E. Sohn, C. Jiao, K. Adler +6 more
R. Mullins, A. Warwick, E. Sohn, A. Lotery
C. Jiao, D. Eliott, C. Spee, Shi-Kun He +4 more
C. Jiao, K. Adler, Xiu-Ying Y. Liu, Wei-Ze Sun +2 more
Ian C. Han, L. Bohrer, K. Gibson-Corley, L. A. Wiley +10 more
E. Sohn, Ian C. Han, M. Abràmoff
Rachel M. Huckfeldt, Jade S. East, E. Stone, E. Sohn
Tien-En Tan, H. W. Chan, Mandeep S. Singh, Tien Y. Wong +4 more
E. Sohn, Austin L Strohbehn, Tomasz P. Stryjewski, K. Brodowska +3 more
E. Chin, David R. P. Almeida, E. Sohn, H. Boldt +4 more
R. Coussa, Elaine M. Binkley, M. Wilkinson, Jeaneen L. Andorf +6 more
E. Sohn, Benjamin C. Chaon, D. Jabs, J. Folk
B. Fenner, S. Whitmore, Adam P. DeLuca, J. L. Andorf +19 more
Erin R. Burnight, B. Fenner, Ian C. Han, Adam P. DeLuca +7 more
Jong G. Park, S. Adrean, Tedi Begaj, A. Capone +34 more
E. Sohn, K. Chirco, J. Folk, R. Mullins
John J. Chen, E. Sohn, J. Folk, V. Mahajan +3 more
E. Perez, David A. Ramirez, Jared D. Peterson, Elaine M. Binkley +7 more
Mark Banghart, Kyungmoo Lee, M. Bahrainian, K. Staggers +7 more
Rion J. Wendland, C. Jiao, S. Russell, Ian C. Han +4 more
R. Coussa, C. Fortenbach, D. Critser, Malia M. Collins +5 more
Erin R. Burnight, L. A. Wiley, Nathaniel K. Mullin, M. Adur +10 more
Ian C. Han, R. Coussa, Mahsaw Mansoor, D. Critser +3 more
E. Sohn, Ian C. Han, B. Roos, Benjamin P. Faga +9 more
Timothy M. Boyce, S. Whitmore, Katayoun Varzavand, S. Russell +4 more