A single CRISPR-Cas9 deletion strategy that targets the majority of DMD patients restores dystrophin function in hiPSC-derived muscle cells
C. Young, Michael R. Hicks, N. Ermolova, H. Nakano +12 more
Researcher profile · Semantic Scholar
C. Young, Michael R. Hicks, N. Ermolova, H. Nakano +12 more
Megan D Hoban, Dianne Lumaquin, C. Kuo, Z. Romero +13 more
Michael R. Hicks, Julia Hiserodt, Katrina I. Paras, W. Fujiwara +9 more
Hai-Bin Xi, J. Langerman, Shan Sabri, P. Chien +13 more
M. Putten, M. Hulsker, C. Young, V. Nadarajah +5 more
C. Young, E. Mokhonova, M. Quiñonez, A. Pyle +1 more
H. Gordish-Dressman, R. Willmann, Laura Dalle Pazze, A. Kreibich +26 more
Hai-Bin Xi, J. Langerman, Shan Sabri, P. Chien +13 more
Michael R. Emami, A. Espinoza, C. Young, Fei-Yang Ma +8 more
Michael R. Hicks, Xiang-Sheng Liu, C. Young, Kholoud K. Saleh +7 more
M. van Putten, C. Young, S. V. D. van den Berg, A. Pronk +6 more
Michael R. Emami, C. Young, Ying Ji, Xiang-Sheng Liu +4 more
D. Rajakumar, C. Almeida, Alexander R. Brinkman, Ding Li +7 more
N. Wein, T. Simmons, D. Rajakumar, D. Lesman +8 more
C. Young, Ekaterina Mokhonova, M. Quiñonez, A. Pyle +1 more
C. Young, Michael R. Hicks, N. Ermolova, H. Nakano +7 more
C. Young, Michael R. Hicks, N. Ermolova, H. Nakano +6 more
C. Kuo, Megan D Hoban, Alok V. Joglekar, C. Young +3 more
Megan D Hoban, Dianne Lumaquin, C. Kuo, Z. Romero +8 more
M. van Putten, M. Hulsker, C. Young, V. Nadarajah +4 more