Skip to content

Home Search Authors Pakistan News Saved

SciRah

SciRah does not host or store research papers. Results come live from free, official scholarly APIs, and every paper links back to its original source.

Data sources

OpenAlex
Semantic Scholar
Crossref
CORE
arXiv
PubMed

Privacy policy Terms of service

Z. Romero · SciRah

Researcher profile · Semantic Scholar

Z. Romero

Share profile

Z. Romero — researcher profile on SciRah

h-index: 17
Works: 37
Citations: 1,384

Most-cited papers

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells.
Megan D Hoban, G. Cost, M. Mendel, Z. Romero +21 more
2015Blood318 citations Open access
Semantic Scholar
CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells.
Megan D Hoban, Dianne Lumaquin, C. Kuo, Z. Romero +13 more
2016Molecular Therapy178 citations Open access
Semantic Scholar
Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome
C. Kuo, Joseph D. Long, Beatriz Campo-Fernández, S. D. De Oliveira +10 more
2018Cell Reports123 citations Open access
Semantic Scholar
Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates.
Z. Romero, A. Lomova, Suzanne Said, A. Miggelbrink +15 more
2019Molecular Therapy112 citations Open access
Semantic Scholar
β-globin gene transfer to human bone marrow for sickle cell disease.
Z. Romero, F. Urbinati, S. Geiger, Aaron R. Cooper +21 more
2013Journal of Clinical Investigation93 citations Open access
Semantic Scholar
Improving Gene Editing Outcomes in Human Hematopoietic Stem and Progenitor Cells by Temporal Control of DNA Repair
A. Lomova, Danielle N. Clark, Beatriz Campo-Fernández, Carmen Flores-Bjurström +10 more
2018Stem Cells89 citations Open access
Semantic Scholar
Human T Cell Generation is Restored in CD3δ Severe Combined Immunodeficiency Through Adenine Base Editing
Grace E. McAuley, G. Yiu, Patrick Chang, Gregory A. Newby +19 more
2023Cell72 citations Open access
Semantic Scholar
High-level correction of the sickle mutation is amplified in vivo during erythroid differentiation
W. Magis, M. DeWitt, S. Wyman, J. Vu +16 more
2018iScience49 citations Open access
Semantic Scholar
Physiological and tissue-specific vectors for treatment of inherited diseases
M. Toscano, Z. Romero, Pilar Muñoz, Marién Cobo +2 more
2011Gene Therapy49 citations Open access
Semantic Scholar
Potentially Therapeutic Levels of Anti-Sickling Globin Gene Expression Following Lentivirus-mediated Gene Transfer in Sickle Cell Disease Bone Marrow CD34+ Cells
F. Urbinati, Philip W. Hargrove, S. Geiger, Z. Romero +7 more
2015Experimental Hematology38 citations Open access
Semantic Scholar
A tissue-specific, activation-inducible, lentiviral vector regulated by human CD40L proximal promoter sequences
Z. Romero, S. Torres, Marién Cobo, Pilar Muñoz +3 more
2011Gene Therapy35 citations Open access
Semantic Scholar
Supramolecular nanosubstrate–mediated delivery system enables CRISPR-Cas9 knockin of hemoglobin beta gene for hemoglobinopathies
Peng Yang, Shih-Jie Chou, Jin-Dian Li, Wen-Qiao Hui +21 more
2020Science Advances34 citations Open access
Semantic Scholar
Promise of gene therapy to treat sickle cell disease
Z. Romero, M. DeWitt, M. Walters
2018Expert Opinion on Biological Therapy26 citations
Semantic Scholar
Characterization of Gene Alterations following Editing of the β-Globin Gene Locus in Hematopoietic Stem/Progenitor Cells.
Joseph D. Long, Megan D Hoban, Aaron R. Cooper, Michael L. Kaufman +7 more
2017Molecular Therapy26 citations Open access
Semantic Scholar
Enrichment of Human Hematopoietic Stem/Progenitor Cells Facilitates Transduction for Stem Cell Gene Therapy
Kismet M Baldwin, F. Urbinati, Z. Romero, Beatriz Campo-Fernández +5 more
2015Stem Cells26 citations Open access
Semantic Scholar
b-globin gene transfer to human bone marrow for sickle cell disease
Z. Romero, F. Urbinati, S. Geiger, Aaron R. Cooper +21 more
201824 citations
Semantic Scholar
The human ankyrin 1 promoter insulator sustains gene expression in a β-globin lentiviral vector in hematopoietic stem cells
Z. Romero, Beatriz Campo-Fernández, J. Wherley, Michael L. Kaufman +9 more
2015Molecular Therapy: Methods & Clinical Development17 citations Open access
Semantic Scholar
In vivo selection for corrected ß-globin alleles after CRISPR/Cas9 editing in human sickle hematopoietic stem cells enhances therapeutic potential
W. Magis, M. DeWitt, S. Wyman, J. Vu +16 more
2018bioRxiv16 citations Open access
Semantic Scholar
Preclinical studies for a phase 1 clinical trial of autologous hematopoietic stem cell gene therapy for sickle cell disease.
F. Urbinati, J. Wherley, S. Geiger, B. C. Fernandez +12 more
2017Cytotherapy16 citations
Semantic Scholar
Delivery of Genome Editing Reagents to Hematopoietic Stem/Progenitor Cells.
Megan D Hoban, Z. Romero, G. Cost, M. Mendel +2 more
2016Current protocols in stem cell biology10 citations
Semantic Scholar
Global and Local Manipulation of DNA Repair Mechanisms to Alter Site-Specific Gene Editing Outcomes in Hematopoietic Stem Cells
Elizabeth Benitez, Anastasia Lomova Kaufman, L. Cervantes, Danielle N. Clark +11 more
2020Frontiers in Genome Editing9 citations Open access
Semantic Scholar
Clinical outcomes of lentiviral vector gene therapy for sickle cell disease
Chattip Prueksapraopong, A. Fernandes, Beatriz Campo-Fernández, Sohini Roy +14 more
2026Blood Advances7 citations Open access
Semantic Scholar
DNA contamination within recombinant adeno-associated virus preparations correlates with decreased CD34+ cell clonogenic potential
Christopher Luthers, S. Ha, Annika Mittelhauser, Marco Morselli +4 more
2024Molecular Therapy: Methods & Clinical Development6 citations Open access
Semantic Scholar
Hematopoietic stem cell gene therapy for the treatment of X-linked agammaglobulinemia
Christopher Luthers, Annika Mittelhauser, A. Colamartino, Xiaomeng Wu +5 more
2025Molecular Therapy: Methods & Clinical Development5 citations
Semantic Scholar
Safer vectors for gene therapy of primary immunodeficiencies.
Z. Romero, M. Toscano, J. D. Unciti, I. Molina +1 more
2009Current Gene Therapy5 citations
Semantic Scholar
Clinical Outcomes of Lenti/G-βAS3-FB Lentiviral Vector Gene Therapy for Sickle Cell Disease
Chattip Prueksapraopong, A. Fernandes, B. C. Fernandez, Sohini Roy +5 more
2025Transplantation and Cellular Therapy2 citations Open access
Semantic Scholar
Oligonucleotide Synthesis Errors Are a Source of Untoward Variation in HDR-Mediated Gene Editing
S. Wyman, Z. Romero, S. Heo, Marian Navarrete +5 more
2025bioRxiv1 citations Open access
Semantic Scholar
Comparative analysis of NSG and NBSGW mice for preclinical evaluation of gene-modified human hematopoietic stem and progenitor cells
C. Kuo, Sean Harrington, Beatriz Campo-Fernández, S. Wyman +10 more
2026Stem cell research & therapeutics0 citations Open access
Semantic Scholar
Development of CRISPR_SCD001, an Autologous Hematopoietic Stem Cell Gene Therapy for Sickle Cell Disease after CRISPR-Cas9 Mediated Correction.
M. DeWitt, Beatriz Campo-Fernández, Sohini Roy, A. L. Kleinhenz +15 more
2026Molecular Therapy0 citations Open access
Semantic Scholar
106 Outcomes Following Hematopoietic Cell Transplant for CD3δ Severe Combined Immune Deficiency: a PIDTC Natural History Study
Tatiana Kalashnikova, Geoff Cuvelier, Brent R. Logan, E. Grunebaum +30 more
2024Clinical Immunology0 citations
Semantic Scholar
S852 IN VIVO SELECTION FOR CORRECTED BETA-GLOBIN ALLELES AFTER CRISPR/CAS9 EDITING IN HUMAN SICKLE HEMATOPOIETIC STEM CELLS ENHANCES THERAPEUTIC POTENTIAL
M. Walters, W. Magis, M. DeWitt, S. Wyman +7 more
2019HemaSphere0 citations Open access
Semantic Scholar
TITLE: High-level correction of the sickle mutation amplified in vivo during erythroid differentiation ONE SENTENCE SUMMARY: Cas9-mediated correction of the sickle mutation in human hematopoietic stem cells can be accomplished at curative levels.
W. Magis, M. DeWitt, S. Wyman, J. Vu +19 more
20190 citations
Semantic Scholar
Using HUDEP Cells as a Model for Gene Editing for -Thalassemia and Sickle Cell Disease
M. Vélez, Julie M. Sanchez, A. Miggelbrink, Z. Romero +1 more
2018Experimental Hematology0 citations Open access
Semantic Scholar
Comparing Two Gene Therapy Approaches for the Treatment of Sickle Cell Disease: Gene Correction vs. Allelic Disruption
Julie M. Sanchez, M. Vélez, A. Miggelbrink, Z. Romero +1 more
2018Experimental Hematology0 citations Open access
Semantic Scholar
118. Characterization of Chromosomal Alterations Using a Zinc-Finger Nuclease Targeting the Beta-Globin Gene Locus in Hematopoietic Stem/Progenitor Cells
Joseph D. Long, Megan D Hoban, C. Kuo, B. C. Fernandez +5 more
20160 citations Open access
Semantic Scholar
338. Evaluation of TALENs and the CRISPR/Cas9 Nuclease System To Correct the Sickle Cell Disease Mutation
Megan D Hoban, Dianne Lumaquin, C. Kuo, Z. Romero +8 more
20150 citations Open access
Semantic Scholar
115. Correction of the Sickle-Cell Disease Mutation in Human Hematopoietic Stem/Progenitor Cells
Megan D Hoban, M. Mendel, Z. Romero, Michael L. Kaufman +21 more
20150 citations Open access
Semantic Scholar

Frequent co-authors

Invite them to SciRah by sharing their profile.

D. Kohn×23
Invite
D. Kohn — researcher profile on SciRah
R. Hollis×17
Invite
R. Hollis — researcher profile on SciRah
Beatriz Campo-Fernández×14
Invite
Beatriz Campo-Fernández — researcher profile on SciRah
Michael L. Kaufman×11
Invite
Michael L. Kaufman — researcher profile on SciRah

Aaron R. Cooper

×11

Invite

Aaron R. Cooper — researcher profile on SciRah

Xiao-Yan Wang×11

Invite

Xiao-Yan Wang — researcher profile on SciRah

Megan D Hoban×10

Invite

Megan D Hoban — researcher profile on SciRah

Invite

F. Urbinati — researcher profile on SciRah

Invite

C. Kuo — researcher profile on SciRah

Joseph D. Long×8

Invite

Joseph D. Long — researcher profile on SciRah

Dianne Lumaquin×7

Invite

Dianne Lumaquin — researcher profile on SciRah

Invite

M. Walters — researcher profile on SciRah