AAV5-miHTT Gene Therapy Demonstrates Broad Distribution and Strong Human Mutant Huntingtin Lowering in a Huntington’s Disease Minipig Model
M. Evers, J. Miniarikova, Š. Juhás, A. Vallès +14 more
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M. Evers, J. Miniarikova, Š. Juhás, A. Vallès +14 more
J. Miniarikova, Ilaria Zanella, A. Huseinovic, Tom van der Zon +8 more
R. Martier, Jolanda M. P. Liefhebber, A. García-Osta, J. Miniarikova +7 more
J. Miniarikova, V. Zimmer, R. Martier, C. Brouwers +9 more
R. Martier, Jolanda M. P. Liefhebber, J. Miniarikova, Tom van der Zon +6 more
J. Miniarikova, M. Evers, P. Konstantinova
K. Cambon, V. Zimmer, Sylvain Martineau, M. Gaillard +10 more
Marina Sogorb-González, J. Miniarikova, Astrid Valles-sanchez, S. V. van Deventer +2 more
Marina Sogorb-González, Carlos Vendrell-Tornero, J. Snapper, A. Stam +9 more
M. Evers, J. Miniarikova, Š. Juhás, A. Vallès +16 more
J. Miniarikova, Marina Sogorb-González, A. Vallès, M. Evers +3 more
J. Klíma, M. Evers, J. Miniarikova, Š. Juhás +15 more
J. Miniarikova, Ilaria Zanella, B. Blits, M. Evers +8 more
M. Evers, J. Miniarikova, B. Blits, Lisa Spronck +9 more
P. Konstantinova, J. Miniarikova, E. Hanenmaaijer, R. Martier +3 more