Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria.
M. Balwani, E. Sardh, P. Ventura, P. Peiró +30 more
Researcher profile · Semantic Scholar
M. Balwani, E. Sardh, P. Ventura, P. Peiró +30 more
Hubert Scharnagl, W. März, Markus Böhm, T. Luger +166 more
H. Oketch-Rabah, A. Roe, C. Rider, H. Bonkovsky +22 more
J. Hoofnagle, H. Bonkovsky, E. Phillips, Yi-Ju Li +15 more
Bruce Wang, H. Bonkovsky, Joseph K. Lim, M. Balwani
H. Scharnagl, W. März, M. Böhm, T. Luger +166 more
H. Bonkovsky, N. Dixon, S. Rudnick
P. Ventura, H. Bonkovsky, L. Gouya, Paula Aguilera‐Peiró +13 more
A. Regev, M. Avigan, A. Kiazand, J. Vierling +18 more
H. Scharnagl, W. März, M. Böhm, T. Luger +166 more
A. Belot, Hervé Puy, I. Hamza, H. Bonkovsky
D. Kuter, H. Bonkovsky, S. Monroy, G. Ross +8 more
R. Vuppalanchi, H. Bonkovsky, J. Ahmad, H. Barnhart +15 more
N. Chalasani, Yi-Ju Li, A. Dellinger, Víctor M. Navarro +10 more
Hubert Scharnagl, W. März, M. Böhm, T. Luger +166 more
K. Anderson, R. Lobo, Denise Z. Salazar, Mary Schloetter +7 more
B. Saberi, Hetanshi Naik, J. Overbey, Angelika L. Erwin +9 more
N. Chalasani, H. Bonkovsky, J. Stine, Jie-Zhun Gu +6 more
C. Majeed, Christopher D Ma, Ted Xiao, S. Rudnick +1 more
N. Dixon, Ting Li, Brandon Marion, Denise Faust +4 more
Rachana K. Gandhi Mehta, J. Caress, S. Rudnick, H. Bonkovsky
A. Honor, S. Rudnick, H. Bonkovsky
Amy K. Dickey, C. Quick, S. Ducamp, Zhao-Zhong Zhu +14 more
M. Balwani, H. Bonkovsky, Cynthia Levy, K. Anderson +5 more
Brenden Chen, S. Whatley, M. Badminton, A. Aarsand +20 more
H. Devarbhavi, M. Ghabril, Huiman Barnhart, Mallikarjun Patil +4 more
S. Massachi, J. Epstein, J. Hurd, H. Bonkovsky
H. Bonkovsky, M. Ghabril, Paola Nicoletti, Andrew Dellinger +7 more
D. Cassiman, R. Kauppinen, S. Monroy, Ming-Jen Lee +7 more
M. Thapar, S. Rudnick, H. Bonkovsky
V. Pulgar, M. Yasuda, L. Gan, R. Desnick +1 more
R. Fontana, D. Kleiner, N. Chalasani, H. Bonkovsky +4 more
R. Vuppalanchi, Yi-Ju Li, Don C. Rockey, Dina Halegoua-DeMarzio +6 more
Christopher D. Ma, Denise Faust, H. Bonkovsky
K. Anderson, R. Desnick, M. F. Stewart, P. Ventura +1 more
M. Balwani, H. Bonkovsky, K. Belongie, Karl E. Anderson +10 more
Q. Binet, C. Miesse, B. Colinet, S. Aydın +45 more
M. Balwani, Hetanshi Naik, J. Overbey, H. Bonkovsky +5 more
Yonatan Edel, P. Stein, H. Kawtharany, A. Aarsand +29 more
M. Thapar, Akash Singh, Kevin M Robinson, H. Bonkovsky
Chaudrey Nasir Majeed, S. Rudnick, H. Bonkovsky
Christopher D. Ma, Denise Faust, H. Bonkovsky
H. Bonkovsky, Christopher D. Ma, Manuela Araque, Jacqueline B. Tiley +2 more
Cynthia Levy, Hetanshi Naik, J. Overbey, Karli Hedstrom +23 more
A. Barritt, Huiman Barnhart, Jie-Zhun Gu, A. Dellinger +2 more
H. Bonkovsky, Sean Rudnick, Christopher D Ma, J. Overbey +7 more
M. Braun-Falco, H. Mankin, Sharon L. Wenger, Stephan DiSean Kendall +187 more
U. Masood, N. Venturini, Paola Nicoletti, Andrew Dellinger +7 more
Amy K Dickey, Sioban Keel, H. Bonkovsky, Karl E. Anderson +6 more