S. Rothenberg

Most-cited papers

1. A Mosaic Activating Mutation in AKT1 Associated with the Proteus Syndrome

   M. Lindhurst, Julie C. Sapp, J. Teer, J. Johnston +36 more

   2011New England Journal of Medicine533 citations Open access

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2. In vivo gene therapy of hemophilia B: sustained partial correction in factor IX-deficient dogs.

   M. Kay, S. Rothenberg, C. N. Landen, D. Bellinger +6 more

   1993Science317 citations

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3. In vivo hepatic gene therapy: complete albeit transient correction of factor IX deficiency in hemophilia B dogs.

   M. A. Kay, C. N. Landen, S. Rothenberg, L. Taylor +9 more

   1994Proceedings of the National Academy of Sciences of the United States of America267 citations Open access

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4. Development of a Clinical Protocol for Hepatic Gene Transfer: Lessons Learned in Preclinical Studies

   F. Ledley, M. Adams, H. Soriano, G. Darlington +13 more

   1993Pediatric Research20 citations

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