Discovery of Risdiplam, a Selective Survival of Motor Neuron-2 ( SMN2) Gene Splicing Modifier for the Treatment of Spinal Muscular Atrophy (SMA).
H. Ratni, M. Ebeling, J. Baird, Stefanie Bendels +24 more
Researcher profile · Semantic Scholar
H. Ratni, M. Ebeling, J. Baird, Stefanie Bendels +24 more
R. Sergott, G. Amorelli, G. Baranello, E. Barreau +19 more
S. Niklaus, S. Albertini, Tobias K. Schnitzer, Nora Denk
Peter M. Maloca, P. Müller, Aaron Y. Lee, A. Tufail +11 more
Nora Denk, Peter M. Maloca, G. Steiner, C. Freichel +3 more
Derrick J. Feenstra, M. Şeleci, Nora Denk, S. Fauser +2 more
Peter M. Maloca, Christine Seeger, H. Booler, P. Valmaggia +9 more
Nora Denk, Peter M. Maloca, G. Steiner, H. Booler +4 more
Peter M. Maloca, M. Pfau, Lucas Janeschitz-Kriegl, Michael Reich +19 more
Peter M. Maloca, C. Freichel, Christof Hänsli, P. Valmaggia +6 more
S. Niklaus, P. Hasler, Tim Bryant, S. Desgent +4 more
Ekaterina A Sokolenko, G. Hilken, Nora Denk, F. Wyss +3 more
Nora Denk, C. Freichel, P. Valmaggia, Nadja Inglin +5 more
Peter M. Maloca, P. Valmaggia, Theresa Hartmann, Marlene Juedes +3 more
C. Bruè, Peter M. Maloca, Catherine-Ann Cukras, P. Valmaggia +1 more
Peter M. Maloca, P. Valmaggia, Nadja Inglin, Beat Hörmann +5 more
Nora Denk, C. Senn, B. Jacobsen, Tobias K. Schnitzer
Nora Denk, C. Senn, Tobias K. Schnitzer, A. Bergadano +4 more