Outcome of patients with classical infantile pompe disease receiving enzyme replacement therapy in Germany.
A. Hahn, Susanne Praetorius, N. Karabul, Johanna Dießel +15 more
2015JIMD Reports60 citations Open access
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A. Hahn, Susanne Praetorius, N. Karabul, Johanna Dießel +15 more