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C. Decker · SciRah

Researcher profile · Semantic Scholar

C. Decker

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C. Decker — researcher profile on SciRah

h-index: 18
Works: 30
Citations: 1,010

Most-cited papers

Long-term follow-up of endurance and safety outcomes during enzyme replacement therapy for mucopolysaccharidosis VI: Final results of three clinical studies of recombinant human N-acetylgalactosamine 4-sulfatase.
P. Harmatz, R. Giugliani, I. Schwartz, N. Guffon +15 more
2008Molecular Genetics and Metabolism206 citations
Semantic Scholar
The Morquio A Clinical Assessment Program: baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects.
P. Harmatz, K. Mengel, R. Giugliani, V. Valayannopoulos +13 more
2013Molecular Genetics and Metabolism142 citations Open access
Semantic Scholar
Enzyme replacement therapy for mucopolysaccharidosis VI: evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase
P. Harmatz, Zi-Fan Yu, R. Giugliani, I. Schwartz +17 more
2010Journal of Inherited Metabolic Disease97 citations Open access
Semantic Scholar
Enzyme replacement therapy for mucopolysaccharidosis VI: long-term cardiac effects of galsulfase (Naglazyme®) therapy
E. Braunlin, H. Rosenfeld, C. Kampmann, J. Johnson +19 more
2012Journal of Inherited Metabolic Disease67 citations Open access
Semantic Scholar
Enzyme replacement therapy for mucopolysaccharidosis VI: Growth and pubertal development in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase
C. Decker, Zi-Fan Yu, R. Giugliani, I. Schwartz +16 more
2010Journal of Pediatric Rehabilitation Medicine65 citations Open access
Semantic Scholar
Galsulfase (Naglazyme®) therapy in infants with mucopolysaccharidosis VI
P. Harmatz, P. Garcia, N. Guffon, L. Randolph +4 more
2013Journal of Inherited Metabolic Disease45 citations Open access
Semantic Scholar
Longitudinal analysis of endurance and respiratory function from a natural history study of Morquio A syndrome.
P. Harmatz, K. Mengel, R. Giugliani, V. Valayannopoulos +14 more
2015Molecular Genetics and Metabolism41 citations Open access
Semantic Scholar
Long-term Immunogenicity of Elosulfase Alfa in the Treatment of Morquio A Syndrome: Results From MOR-005, a Phase III Extension Study.
B. Long, T. Tompkins, C. Decker, Lynne A. Jesaitis +5 more
2017Clinical Therapeutics33 citations Open access
Semantic Scholar
Impact of long-term elosulfase alfa on activities of daily living in patients with Morquio A syndrome in an open-label, multi-center, phase 3 extension study.
C. Hendriksz, R. Parini, M. AlSayed, J. Raiman +10 more
2017Molecular Genetics and Metabolism33 citations Open access
Semantic Scholar
Biomarker analysis of Morquio syndrome: identification of disease state and drug responsive markers
Lisa Argento Martell, Kelly Lau, M. Mei, Vicki Burnett +2 more
2011Orphanet Journal of Rare Diseases33 citations Open access
Semantic Scholar
Impact of long-term elosulfase alfa treatment on respiratory function in patients with Morquio A syndrome
C. Hendriksz, K. Berger, R. Parini, M. AlSayed +11 more
2016Journal of Inherited Metabolic Disease32 citations Open access
Semantic Scholar
Long-term safety and efficacy of pegvaliase for the treatment of phenylketonuria in adults: combined phase 2 outcomes through PAL-003 extension study
N. Longo, R. Zori, M. Wasserstein, J. Vockley +7 more
2018Orphanet Journal of Rare Diseases28 citations Open access
Semantic Scholar
Impact of elosulfase alfa in patients with morquio A syndrome who have limited ambulation: An open‐label, phase 2 study
P. Harmatz, E. Mengel, T. Geberhiwot, N. Muschol +8 more
2016American Journal of Medical Genetics. Part A28 citations Open access
Semantic Scholar
Safety, immunogenicity, and clinical outcomes in patients with Morquio A syndrome participating in 2 sequential open-label studies of elosulfase alfa enzyme replacement therapy (MOR-002/MOR-100), representing 5 years of treatment.
C. Hendriksz, S. Santra, S. Jones, T. Geberhiwot +5 more
2018Molecular Genetics and Metabolism27 citations Open access
Semantic Scholar
Pegvaliase for the treatment of phenylketonuria: Results of the phase 2 dose-finding studies with long-term follow-up.
B. Burton, N. Longo, J. Vockley, D. Grange +7 more
2020Molecular Genetics and Metabolism25 citations Open access
Semantic Scholar
Induction, titration, and maintenance dosing regimen in a phase 2 study of pegvaliase for control of blood phenylalanine in adults with phenylketonuria.
R. Zori, Janet A. Thomas, N. Shur, W. Rizzo +6 more
2018Molecular Genetics and Metabolism25 citations
Semantic Scholar
Long Term Outcomes of a Phase 1/2, Multicenter, Open-Label, Dose-Escalation Study to Evaluate the Safety, Tolerability, and Efficacy of BMN 110 in Patients with Mucopolysaccharidosis IVA (Morquio A Syndrome)
C. Hendriksz, A. Vellodi, S. Jones, H. Takkele +3 more
201225 citations
Semantic Scholar
Successful Management of Difficult Infusion-Associated Reactions in a Young Patient With Mucopolysaccharidosis Type VI Receiving Recombinant Human Arylsulfatase B (Galsulfase [Naglazyme])
Katherine H. Kim, C. Decker, B. Burton
2008Pediatrics25 citations
Semantic Scholar
Antibodies that neutralize cellular uptake of elosulfase alfa are not associated with reduced efficacy or pharmacodynamic effect in individuals with Morquio A syndrome.
Andrew C. Melton, R. Soon, T. Tompkins, B. Long +8 more
2017JIM - Journal of Immunological Methods17 citations Open access
Semantic Scholar
Relationship Between Patient-Reported Outcomes and Clinical Outcomes in Patients With Morquio A Syndrome
C. Lampe, Mohit J. Jain, A. Olaye, B. Meesen +2 more
201513 citations Open access
Semantic Scholar
BMN 110 (Recombinant Human GALNS), an Investigational Enzyme Replacement Therapy for Mucopolysaccharidosis Type IVA (MPS IVA Or Morquio Syndrome), Promotes Type II Collagen Synthesis in MPS IVA Patients
F. Lorget, Sungwook Lee, Kelly Lau, L. Tsuruda +6 more
20123 citations
Semantic Scholar
Elosulfase alfa treatment and changes in physical functioning and disability in Morquio syndrome type A
C. Hendriksz, R. Parini, M. Al-Sayed, J. Raiman +10 more
20171 citations
Semantic Scholar
Interim analysis of palladium: A phase 4 study to evaluate a rapid drug desensitization protocol for adults receiving pegvaliase
K. Lindstrom, R. Batabyal, T. R. Lal, L. Allan +9 more
2026Molecular Genetics and Metabolism0 citations
Semantic Scholar
DESIGN OF A GLOBAL, MULTICENTER STUDY TO ASSESS MATERNAL, FETAL, AND INFANT OUTCOMES OF PEGVALIASE EXPOSURE DURING PREGNANCY AND BREASTFEEDING
G. Clague, N. Longo, C. Decker, Joellen Hunt +1 more
2023Molecular Genetics and Metabolism0 citations
Semantic Scholar
Safety, efficacy, and immunogenicity of elosulfase alfa in patients with Morquio syndrome type A participating in 2 sequential open-label studies (MOR-002/MOR-100), representing 5 years of treatment
C. Hendriksz, S. Santra, S. Jones, T. Geberhiwot +5 more
20180 citations
Semantic Scholar
Impact of elosulfase alfa in patients with Morquio syndrome type A who have limited ambulation: An open-label, phase 2 study
P. Harmatz, A. Jester, E. Mengel, M. Treadwell +6 more
20160 citations
Semantic Scholar
Galsulfase (Naglazyme®) therapy in infants with mucopolysaccharidosis
P. Harmatz, P. García, N. Guffon, L. Randolph +4 more
20140 citations
Semantic Scholar
Keratan sulfate (KS) analysis in patients with Morquio syndrome type A: LC-MS/MS analysis of KS disaccharides demonstrates that urine is a better source than plasma to monitor dynamic change in KS
N. Miller, G. Taniguchi, C. Decker, Huiyu Zhou +2 more
20140 citations Open access
Semantic Scholar
Establishing a biomarker research working group for the mucopolysaccharidoses
G. Cox, C. Decker, P. Haslett, R. Mankoski +4 more
20130 citations
Semantic Scholar
60. A multicenter, multinational, cross-sectional clinical assessment study of subjects with mucopolysaccharidosis IVA (Morquio syndrome)
C. Henkel, C. Decker, Monica L Miller
20100 citations
Semantic Scholar

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P. Harmatz — researcher profile on SciRah
C. Hendriksz×11
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B. Burton×10
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R. Giugliani×9
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