article
Long-term kidney and liver outcome in 50 children with autosomal recessive polycystic kidney disease
Guillaume Dorvala b c✉, Olivia Boyerc d, Anne Couderce, Jean‐Daniel Delbetf, Laurence Heidetc d, Dominique Debrayg, Pauline Krugc d, Muriel Girardg, Brigitte Llanash, Marina Charbitc d, Saoussen Kridc d, Nathalie Biebuyckc d, Marc Filai, Cécile Courivaudj, Frances Tilleyk, Nicolas Garcelonl, Thomas Blancm, Christophe Chardotm, Rémi Salomonc d, Florence Lacailleg
- aDepartment of Pediatric Nephrology, MARHEA Reference Center, Hôpital Universitaire Necker-Enfants Malades, AP-HP, 149 Rue de Sèvres, 75015, Paris, France. guillaume.dorval@inserm.fr
- bImagine Institute, Université de Paris, Paris, France. guillaume.dorval@inserm.fr
- cDepartment of Pediatric Nephrology, MARHEA Reference Center, Hôpital Universitaire Necker-Enfants Malades, AP-HP, 149 Rue de Sèvres, 75015, Paris, France
- dImagine Institute, Université de Paris, Paris, France
- eDepartment of Pediatric Nephrology, Robert Debré Hospital, AP-HP, Paris, France
- fDepartment of Pediatric Nephrology, Armand Trousseau Hospital, AP-HP, Paris, France
- gDepartment of Gastroenterology-Hepatology-Nutrition, Reference Center for Biliary Atresia and Cholestatic Genetic Diseases, Hôpital Universitaire Necker-Enfants Malades, AP-HP, Paris, France
- hDepartment of Pediatric Nephrology, Hôpital Universitaire Pellegrin, Bordeaux, France
- iDepartment of Pediatric Nephrology, Centre Hospitalier Régional Universitaire de Montpellier, Montpellier, France
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Abstract
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TL;DRLong-term outcome in patients with ARPKD is heterogeneous, and in this cohort did not depend on age at diagnosis except for blood pressure, and few patients required liver transplantation. (Semantic Scholar)

